Pharmaceutical Executive

← Pharmaceutical Executive3 Sept · 3 min

Pharmaceutical Executive Daily: Ultragenyx's Apazunersen Fails Phase III Trial

Pharmaceutical Executive Daily: Ultragenyx's Apazunersen Fails Phase III Trial3 Sept3 min

Ultragenyx shares plunge after apazunersen fails its Phase III trial in Angelman syndrome, Mark Cziraky of Carelon Research talks through the mechanics of analyzing linked real-world data sets, and Melanie Whittington joins The Ron Lanton Report to argue biopharma policy needs to stay tethered to patients, not abstractions.